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Thipparat Suwanmanee

Observed name: Suwanmanee, Thipparat
OpenAlex ID: A5005983005
Employing a Gain-of-Function Factor IX Variant R338L to Advance the Efficacy and Safety of Hemophilia B Human Gene Therapy: Preclinical Evaluation Supporting an Ongoing Adeno-Associated Virus Clinical Trial
2014 · Paul E. Monahan, Junjiang Sun, et al. · Human Gene Therapy · 108
RNA repair restores hemoglobin expression in IVS2–654 thalassemic mice
2009 · Saovaros Svasti, Thipparat Suwanmanee, et al. · Proceedings of the National Academy of Sciences · 79
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Repair of a Splicing Defect in Erythroid Cells from Patients with β-Thalassemia/HbE Disorder
2002 · Thipparat Suwanmanee, Halina Sierakowska, et al. · Molecular Therapy · 76
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Restoration of Human β-Globin Gene Expression in Murine and Human IVS2–654 Thalassemic Erythroid Cells by Free Uptake of Antisense Oligonucleotides
2002 · Thipparat Suwanmanee, Halina Sierakowska, et al. · Molecular Pharmacology · 66
Gene therapy knockdown of VEGFR2 in retinal endothelial cells to treat retinopathy
2018 · Aaron B. Simmons, Colin A. Bretz, et al. · Angiogenesis · 61
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Targeted Knockdown of Overexpressed VEGFA or VEGF164 in Müller cells maintains retinal function by triggering different signaling mechanisms
2018 · Silke Becker, Haibo Wang, et al. · Scientific Reports · 49
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Integration-deficient Lentiviral Vectors Expressing Codon-optimized R338L Human FIX Restore Normal Hemostasis in Hemophilia B Mice
2013 · Thipparat Suwanmanee, Genlin Hu, et al. · Molecular Therapy · 44
Toward Personalized Gene Therapy: Characterizing the Host Genetic Control of Lentiviral-Vector-Mediated Hepatic Gene Delivery
2017 · Thipparat Suwanmanee, Martin T. Ferris, et al. · Molecular Therapy — Methods & Clinical Development · 19
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Superior lentiviral vectors designed for BSL-0 environment abolish vector mobilization
2018 · Peirong Hu, Yanmin Bi, et al. · Gene Therapy · 15
Intravenously administered LV-169 delivers a functional BCMA-CAR transgene to niche-resident T cells and leads to elimination of disseminated myeloma in MHC-deficient NSG mice
2025 · Stephen Russell, Gopal Naik Nenavath, et al. · Blood · 4
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Correction to: Gene therapy knockdown of VEGFR2 in retinal endothelial cells to treat retinopathy
2018 · Aaron B. Simmons, Colin A. Bretz, et al. · Angiogenesis · 3
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Abstract 150: T-cell specific transcriptional control eliminates CAR-mediated off-target transduction by CD3-retargeted lentiviral vectors, enabling safe in vivo generation of potent αBCMA-CAR T cells.
2026 · Karina Krotova, Nandakumar Packiriswamy, et al. · Cancer Research
Abstract 273: High-avidity reversible engager proteins efficiently redirect the entry of intravenously delivered lentiviral vectors, simplifying the direct in vivo delivery of CAR-T cell therapy.
2026 · Gopal Naik Nenavath, Nandakumar Packiriswamy, et al. · Cancer Research
Correction to: Gene therapy knockdown of VEGFR2 in retinal endothelial cells to treat retinopathy
2025 · Yang, Zhihong, Kunz, Eric, et al. · Carolina Digital Repository (University of North Carolina at Chapel Hill)
Knockdown of the erythropoietin receptor in endothelial cells extends physiological retinal vascular development in a model of retinopathy of prematurity
2019 · Aaron B. Simmons, Eric Kunz, et al. · Investigative Ophthalmology & Visual Science
Endothelial Cell STAT3 Knockdown Inhibits Intravitreal Neovascularization in a Rat Model of Oxygen Induced Retinopathy
2018 · Colin A. Bretz, Eric Kunz, et al. · Investigative Ophthalmology & Visual Science
Knockdown of endothelial cell VEGFR2 reduces intravitreal neovascularization in the rat model of Retinopathy of Prematurity
2018 · Aaron B. Simmons, Eric Kunz, et al. · Investigative Ophthalmology & Visual Science
Works count: 17
Citation count: 524
H-index: 9
I10-index: 9
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