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Jason Skowronski
Observed name:
Skowronski, Jason
Observed institution:
Stanford University
ORCID:
0000-0002-2241-1148
Observed ORCID:
0000-0002-2241-1148
OpenAlex ID:
A5023100896
Development of β-globin gene correction in human hematopoietic stem cells as a potential durable treatment for sickle cell disease
2021
·
Annalisa Lattanzi
, Joab Camarena
, et al.
·
Science Translational Medicine
·
171
One Year Follow-up on the First Patient Treated with Nula-Cel: An Autologous CRISPR/Cas9 Gene Corrected CD34+ Cell Product to Treat Sickle Cell Disease
2023
·
David C Shyr
, Robert Lowsky
, et al.
·
Blood
·
29
Molecular dynamics of genome editing with CRISPR-Cas9 and rAAV6 virus in human HSPCs to treat sickle cell disease
2023
·
Liwen Xu
, Premanjali Lahiri
, et al.
·
Molecular Therapy — Methods & Clinical Development
·
16
Functional screening in human HSPCs identifies optimized protein-based enhancers of Homology Directed Repair
2024
·
Juan A. Perez-Bermejo
, Oghene Efagene
, et al.
·
Nature Communications
·
9
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Works count:
5
Citation count:
225
H-index:
4
I10-index:
3
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