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Fabiola De Mattia

Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded access
2022 · Francesca Fumagalli, Valeria Calbi, et al. · The Lancet · 299
Cross-Talk between AURKA and Plk1 in Mitotic Entry and Spindle Assembly
2015 · Italia Anna Asteriti, Fabiola De Mattia, et al. · Frontiers in Oncology · 102
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NuMA Phosphorylation by Aurora-A Orchestrates Spindle Orientation
2016 · Sara Gallini, Manuel Carminati, et al. · Current Biology · 93
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Long-term lineage commitment in haematopoietic stem cell gene therapy
2024 · Andrea Calabria, Giulio Spinozzi, et al. · Nature · 52
The Aurora-A inhibitor MLN8237 affects multiple mitotic processes and induces dose-dependent mitotic abnormalities and aneuploidy
2014 · Italia Anna Asteriti, Erica Di Cesare, et al. · Oncotarget · 50
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Long-Term Effects of Atidarsagene Autotemcel for Metachromatic Leukodystrophy
2025 · Francesca Fumagalli, Valeria Calbi, et al. · New England Journal of Medicine · 34
Leukocyte and Dried Blood Spot Arylsulfatase A Assay by Tandem Mass Spectrometry
2020 · Xinying Hong, Arun Babu Kumar, et al. · Analytical Chemistry · 34
Hematopoietic Tumors in a Mouse Model of X-linked Chronic Granulomatous Disease after Lentiviral Vector-Mediated Gene Therapy
2020 · Raisa Jofra Hernández, Andrea Calabria, et al. · Molecular Therapy · 22
Biological and functional characterization of bone marrow-derived mesenchymal stromal cells from patients affected by primary immunodeficiency
2017 · Nadia Starc, Daniela Ingo, et al. · Scientific Reports · 17
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Lentiviral hematopoietic stem and progenitor cell gene therapy (HSPC-GT) for metachromatic leukodystrophy (MLD): Clinical outcomes from 33 patients
2020 · Francesca Fumagalli, Valeria Calbi, et al. · Molecular Genetics and Metabolism · 11
Lentiviral haematopoietic stem cell gene therapy for metachromatic leukodystrophy: Results in nine patients treated with a cryopreserved formulation of OTL-200
2021 · Valeria Calbi, Francesca Fumagalli, et al. · Molecular Genetics and Metabolism · 4
P005: Atidarsagene autotemcel (hematopoietic stem cell–gene therapy) preserves cognitive and motor development in metachromatic leukodystrophy with up to 12 years follow-up*
2024 · Francesca Fumagalli, Valeria Calbi, et al. · Genetics in Medicine Open · 1
Long-term clinical outcomes of atidarsagene autotemcel (autologous hematopoietic stem cell gene therapy [HSC-GT] for metachromatic leukodystrophy) with up to 11 years follow-up
2023 · Francesca Fumagalli, Valeria Calbi, et al. · Molecular Genetics and Metabolism · 1
Lentiviral Hematopoietic Stem and Progenitor Cell Gene Therapy for Metachromatic Leukodystrophy (MLD): Clinical Outcomes from 38 Patients
2021 · Mirko Essing, Alberto Zambon, et al. · Neuropediatrics · 1
Lentiviral hematopoietic stem cell gene therapy (atidarsagene autotemcel) for late juvenile metachromatic leukodystrophy (MLD)
2024 · Vera Gallo, Valeria Calbi, et al. · Molecular Genetics and Metabolism
Atidarsagene autotemcel (autologous hematopoietic stem cell gene therapy) preserves cognitive and motor development in early-onset metachromatic leukodystrophy with up to 12 years follow-up
2024 · Francesca Fumagalli, Valeria Calbi, et al. · Molecular Genetics and Metabolism
Lentiviral haematopoietic stem cell gene therapy for metachromatic leukodystrophy: Results in 5 patients treated under nominal compassionate use
2023 · Valeria Calbi, Francesca Fumagalli, et al. · Molecular Genetics and Metabolism
Blood sulfatides as disease biomarker for metachromatic leukodystrophy: Disease characterization, early diagnosis, and response to treatment
2023 · Valeria Calbi, Francesca Fumagalli, et al. · Molecular Genetics and Metabolism
Adaptive Routes of Hematopoietic Stem Cell Differentiation to Disease Conditions and Age in Gene Therapy Patients
2022 · Andrea Calabria, Giulio Spinozzi, et al. · Blood
Hematopoietic Tumors in a Mouse Model of X-linked Chronic Granulomatous Disease after Lentiviral Vector-Mediated Gene Therapy
2022 · Jofra Hernández, Raisa, Calabria, Andrea, et al. · Zenodo (CERN European Organization for Nuclear Research)
Works count: 20
Citation count: 721
H-index: 10
I10-index: 10
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