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Author

Gerard J. Platenburg

Observed names: G Platenburg, G. Platenburg, G.J. Platenburg, Gerard Platenburg, Platenburg, G, Platenburg, G., Platenburg, Gerard
Observed institutions: Leiden University, Netherlands Organisation for Applied Scientific Research, Amsterdam UMC Location University of Amsterdam, ISA Pharmaceuticals (Netherlands), ProQR Therapeutics (Netherlands), Pharming Group (Netherlands)
ORCID: 0000-0003-3499-7542
Observed ORCID: 0000-0003-3499-7542
OpenAlex ID: A5056174073
Local Dystrophin Restoration with Antisense Oligonucleotide PRO051
2007 · Judith C. van Deutekom, Anneke A. Janson, et al. · New England Journal of Medicine · 798
Systemic Administration of PRO051 in Duchenne's Muscular Dystrophy
2011 · Nathalie M. Goemans, Mar Tulinius, et al. · New England Journal of Medicine · 696
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Generation Of Transgenic Dairy Cattle Using ‘in vitro’ Embryo Production
1991 · Paul Krimpenfort, Adriana Rademakers, et al. · Nature Biotechnology · 300
Triplet-repeat oligonucleotide-mediated reversal of RNA toxicity in myotonic dystrophy
2009 · Susan A. M. Mulders, Walther J. A. A. van den Broek, et al. · Proceedings of the National Academy of Sciences · 276
Effect of an intravitreal antisense oligonucleotide on vision in Leber congenital amaurosis due to a photoreceptor cilium defect
2018 · Artur V. Cideciyan, Samuel G. Jacobson, et al. · Nature Medicine · 228
In vivo comparison of 2′‐O‐methyl phosphorothioate and morpholino antisense oligonucleotides for Duchenne muscular dystrophy exon skipping
2009 · Hans A. Heemskerk, Christa L. de Winter, et al. · The Journal of Gene Medicine · 177
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Intravitreal Sepofarsen for Leber Congenital Amaurosis Type 10 (LCA10)
2020 · Stephen R. Russell, Arlene V. Drack, et al. · Nature Medicine · 155
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Antisense oligonucleotide-based treatment of retinitis pigmentosa caused by USH2A exon 13 mutations
2021 · Kalyan Dulla, Ralph Slijkerman, et al. · Molecular Therapy · 152
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Expression of human lactoferrin in milk of transgenic mice
1994 · Gerard J. Platenburg, Erika P. A. Kootwijk, et al. · Transgenic Research · 111
Vaccine-Induced Effector-Memory CD8+ T Cell Responses Predict Therapeutic Efficacy against Tumors
2012 · Suzanne van Duikeren, Marieke F Fransen, et al. · The Journal of Immunology · 97
Generation of Transgenic Mice and Germline Transmission of a Mammalian Artificial Chromosome Introduced into Embryos by Pronuclear Microinjection
2000 · Deborah O. Co, Anita H. Borowski, et al. · Chromosome Research · 87
Butyrate stimulates tissue-type plasminogen-activator synthesis in cultured human endothelial cells
1987 · T Kooistra, J van den Berg, et al. · Biochemical Journal · 81
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Targeted pseudouridylation: An approach for suppressing nonsense mutations in disease genes
2023 · Hironori Adachi, Yi Pan, et al. · Molecular Cell · 69
Production of recombinant human type I procollagen homotrimer in the mammary gland of transgenic mice
1999 · P. David Toman, Frank Pieper, et al. · Transgenic Research · 69
QR-313, an Antisense Oligonucleotide, Shows Therapeutic Efficacy for Treatment of Dominant and Recessive Dystrophic Epidermolysis Bullosa: A Preclinical Study
2020 · Olivier Bornert, Marieke Hogervorst, et al. · Journal of Investigative Dermatology · 57
Antisense oligonucleotide therapy corrects splicing in the common Stargardt disease type 1-causing variant ABCA4 c.5461-10T>C
2023 · Melita Kaltak, Petra de Bruijn, et al. · Molecular Therapy — Nucleic Acids · 46
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Evaluation of eluforsen, a novel RNA oligonucleotide for restoration of CFTR function in in vitro and murine models of p.Phe508del cystic fibrosis
2019 · Wouter Beumer, Jim Swildens, et al. · PLoS ONE · 30
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Synthesis and in Vitro Evaluation of PNA−Peptide−DETA Conjugates as Potential Cell Penetrating Artificial Ribonucleases
2004 · Lene Petersen, Martijn C. de Koning, et al. · Bioconjugate Chemistry · 30
Characterization of HLA DR3/DQ2 transgenic mice: a potential humanized animal model for autoimmune disease studies
2002 · Dan Chen, Roanna Ueda, et al. · European Journal of Immunology · 30
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Mammary gland-specific hypomethylation ofHpa II sites flanking the bovine αS1-casein gene
1996 · Gerard J. Platenburg, Ellen J. Vollebregt, et al. · Transgenic Research · 22
High-level expression of bovine αs1-casein in milk of transgenic mice
1998 · MONIQUE Rijnkels, Patricia M. Kooiman, et al. · Transgenic Research · 18
A pathogenic proteolysis–resistant huntingtin isoform induced by an antisense oligonucleotide maintains huntingtin function
2022 · Hyeongju Kim, Sophie Lenoir, et al. · JCI Insight · 14
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QR-1011 restores defective ABCA4 splicing caused by multiple severe ABCA4 variants underlying Stargardt disease
2024 · Melita Kaltak, Petra de Bruijn, et al. · Scientific Reports · 10
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Stargardt disease-associated in-frame ABCA4 exon 17 skipping results in significant ABCA4 function
2023 · Melita Kaltak, Rocio Blanco-Garavito, et al. · Journal of Translational Medicine · 10
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Antisense-mediated exon skipping to correct IL-12Rβ1 deficiency in T cells
2009 · Esther van de Vosse, Els M. Verhard, et al. · Blood · 10
Works count: 54
Citation count: 3,588
H-index: 20
I10-index: 25
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