Author

Daniel Ferretti

Observed name: Daniel M. Ferretti

Institution: Biogen (United States)

Observed institution: Biogen (United States)

OpenAlex ID: A5061561968

In vivo genome editing using novel AAV-PHP variants rescues motor function deficits and extends survival in a SOD1-ALS mouse model

2022 · Yi A. Chen, Mark W. Kankel, et al. · Gene Therapy · 30

Efficacy and safety of a SOD1-targeting artificial miRNA delivered by AAV9 in mice are impacted by miRNA scaffold selection

2023 · Shukkwan K. Chen, Zachary C.E. Hawley, et al. · Molecular Therapy — Nucleic Acids · 26

Temporal Progression of Excitotoxic Calcium Following Distal Middle Cerebral Artery Occlusion in Freely Moving Mice

2020 · Ashley N. Nelson, Michael S. Calhoun, et al. · Frontiers in Cellular Neuroscience · 9

Viral-mediated knockdown of Atxn2 attenuates TDP-43 pathology and muscle dysfunction in the PFN1C71G ALS mouse model

2025 · Zachary C. E. Hawley, Xueying Li, et al. · Acta Neuropathologica Communications · 2

Antisense oligonucleotide treatment following viral delivery of artificial SOD1-targeting miRNA shows improved efficacy in SOD1-G93A mice

2026 · Zachary C.E. Hawley, Amanda J. Guise, et al. · Molecular Therapy Advances

Lumbar Intrathecal Injection of SOD1-ASOs for Precise CNS Targeting and Predictive Efficacy in Human SOD1-G93A ALS Mice

2026 · Twinkle Chowdhury, Shanmugam Muruganandan, et al. · Journal of Visualized Experiments

Works count: 6

Citation count: 67

H-index: 3

I10-index: 2