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Paula S. Montenegro-Miranda

Observed names: Montenegro Miranda, Paula S., P S Montenegro-Miranda, Paula Montenegro Miranda, Paula Montenegro-Miranda, Paula S. Miranda
OpenAlex ID: A5079487161
A Protocol for Lentiviral Transduction and Downstream Analysis of Intestinal Organoids
2015 · Jooske F. Van Lidth de Jeude, Jacqueline L. M. Vermeulen, et al. · Journal of Visualized Experiments · 81
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Intrastriatal Administration of AAV5-miHTT in Non-Human Primates and Rats Is Well Tolerated and Results in miHTT Transgene Expression in Key Areas of Huntington Disease Pathology
2021 · Elisabeth Spronck, Astrid Vallès, et al. · Brain Sciences · 47
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A Novel Organoid Model of Damage and Repair Identifies HNF4α as a Critical Regulator of Intestinal Epithelial Regeneration
2020 · Paula S. Montenegro-Miranda, Jonathan H.M. van der Meer, et al. · Cellular and Molecular Gastroenterology and Hepatology · 39
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Mycophenolate Mofetil Impairs Transduction of Single-Stranded Adeno-Associated Viral Vectors
2011 · Paula S. Montenegro-Miranda, Lysbeth ten Bloemendaal, et al. · Human Gene Therapy · 35
Towards Liver-Directed Gene Therapy for Crigler-Najjar Syndrome
2009 · Paula Montenegro Miranda, Piter Bosma · Current Gene Therapy · 35
Enhanced Factor IX Activity following Administration of AAV5-R338L “Padua” Factor IX versus AAV5 WT Human Factor IX in NHPs
2019 · Elisabeth A. Spronck, Ying Poi Liu, et al. · Molecular Therapy — Methods & Clinical Development · 34
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Polyinosinic Acid Blocks Adeno-Associated Virus Macrophage Endocytosis In Vitro and Enhances Adeno-Associated Virus Liver-Directed Gene Therapy In Vivo
2013 · Remco van Dijk, Paula S. Montenegro-Miranda, et al. · Human Gene Therapy · 29
A Protocol for Lentiviral Transduction and Downstream Analysis of Intestinal Organoids
2015 · Jooske F. Van Lidth de Jeude, Jacqueline L. M. Vermeulen, et al. · Journal of Visualized Experiments · 27
Adeno-Associated Viral Vector Serotype 5 Poorly Transduces Liver in Rat Models
2013 · Paula S. Montenegro-Miranda, Astrid Pañeda, et al. · PLoS ONE · 18
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In the rat liver, Adenoviral gene transfer efficiency is comparable to AAV
2013 · P S Montenegro-Miranda, V Pichard, et al. · Gene Therapy · 18
Overexpression of insulin like growth factor binding protein 5 reduces liver fibrosis in chronic cholangiopathy
2012 · Aleksandar Sokolović, Paula S. Montenegro-Miranda, et al. · Biochimica et Biophysica Acta (BBA) - Molecular Basis of Disease · 14
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Preclinical efficacy and safety of adeno-associated virus 5 alpha-galactosidase: A gene therapy for Fabry disease
2024 · Jolanda M.P. Liefhebber, Giso Brasser, et al. · Molecular Therapy — Methods & Clinical Development · 9
Ezetimibe: A biomarker for efficacy of liver directed UGT1A1 gene therapy for inherited hyperbilirubinemia
2012 · Paula S. Montenegro-Miranda, Nina Sneitz, et al. · Biochimica et Biophysica Acta (BBA) - Molecular Basis of Disease · 6
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Polyinosinic acid blocks adeno-associated virus macrophage endocytosis in vitro and enhances adeno-associated virus liver directed gene therapy in vivo
2013 · Remco van Dijk, Paula Montenegro-Miranda, et al. · Human Gene Therapy Methods · 1
Efficacy of AAV5-GLA gene therapy in manifest Fabry disease mice
2023 · Jolanda M.P. Liefhebber, Giso Brasser, et al. · Molecular Genetics and Metabolism
THU-363-Lipid nanoparticle pre-treatment improves adeno-associated virus diffusion in the primate liver and enables an increase of therapeutic transgene expression
2019 · Karin L Kwikkers, Lukas Schwarz, et al. · Journal of Hepatology
Predictable Protein Expression with Enhanced Factor IX Activity Following Administration of a Modified AAV5-hFIX Vector to Nonhuman Primates
2017 · Ying Poi Liu, Jacek Lubelski, et al. · Blood
Works count: 18
Citation count: 393
H-index: 11
I10-index: 11
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