Author

Susan Tom

Institution: Sangamo BioSciences (United States)

Observed institutions: University of Vermont, Tulane University, University of Washington, Albany Molecular Research (United States), Sangamo BioSciences (United States), Louisiana State University Health Sciences Center New Orleans

OpenAlex ID: A5083375634

Adult stem cells from bone marrow stroma differentiate into airway epithelial cells: Potential therapy for cystic fibrosis

2004 · Guoshun Wang, Bruce A. Bunnell, et al. · Proceedings of the National Academy of Sciences · 281

Dose-Dependent Prevention of Metabolic and Neurologic Disease in Murine MPS II by ZFN-Mediated In Vivo Genome Editing

2018 · Kanut Laoharawee, Russell C. DeKelver, et al. · Molecular Therapy · 125

ZFN-Mediated In Vivo Genome Editing Corrects Murine Hurler Syndrome

2018 · Li Ou, Russell C. DeKelver, et al. · Molecular Therapy · 84

RNA-binding Protein Muscleblind-like 3 (MBNL3) Disrupts Myocyte Enhancer Factor 2 (Mef2) β-Exon Splicing

2010 · Kyung-Soon Lee, Yi Cao, et al. · Journal of Biological Chemistry · 44

The design and synthesis of novel SGLT2 inhibitors: C-glycosides with benzyltriazolopyridinone and phenylhydantoin as the aglycone moieties

2014 · Cheng Guo, Min Hu, et al. · Bioorganic & Medicinal Chemistry · 43

ZFN-mediated genome editing of albumin “safe harbor” in vivo results in supraphysiological levels of human IDS, IDUA and GBA in mice

2015 · Russell DeKelver, Michelle Rohde, et al. · Molecular Genetics and Metabolism · 3

479. ZFN-Mediated In Vivo Genome Editing Results in Supraphysiological Levels of Lysosomal Enzymes Deficient in Hunter and Hurler Syndrome and Gaucher Disease

2015 · Thomas Wechsler, Russel DeKelver, et al. · Molecular Therapy · 2

ZFN-mediated in vivo genome editing of hepatocytes results in phenotypic correction in murine MPS I and MPS II models

2018 · Thomas Wechsler, Russell DeKelver, et al. · Molecular Genetics and Metabolism · 1

ZFN-mediated in vivo genome editing results in phenotypic correction in murine MPS I and MPS II models

2017 · Russell DeKelver, Li Ou, et al. · Molecular Genetics and Metabolism · 1

484. In Vivo Zinc-Finger Nuclease Mediated Iduronate-2-Sulfatase (IDS) Target Gene Insertion and Correction of Metabolic Disease in a Mouse Model of Mucopolysaccharidosis Type II (MPS II)

2016 · Kanut Laoharawee, Russell DeKelver, et al. · Molecular Therapy · 1

485. ZFN-Mediated Liver-Targeting Gene Therapy Corrects Systemic and Neurological Disease of Mucopolysaccharidosis Type I

2016 · Li Ou, Russell DeKelver, et al. · Molecular Therapy · 1

ZFN-mediated correction of murine MPS I model by expression of the human IDUA cDNA from the albumin “safe harbor” locus

2016 · Li Ou, Russell DeKelver, et al. · Molecular Genetics and Metabolism · 1

Monoclonal Antibodies Against Muscleblind-like 3, a Protein with Punctate Nuclear Localization

2011 · Kyung-Soon Lee, K.A. Lewis, et al. · Hybridoma · 1

ZFN-mediated in vivo genome editing results in supraphysiological levels of human iduronate 2-sulfatase and phenotypic correction in a murine MPS II model

2016 · Russell DeKelver, Kanut Laoharawee, et al. · Molecular Genetics and Metabolism

Works count: 14

Citation count: 588

H-index: 5

I10-index: 5