Author

Kathryn Koszka

Institution: Biogen (United States)

Observed institutions: Broad Institute, Stowers Institute for Medical Research, Biogen (United States), Howard Hughes Medical Institute, Harvard University, Harvard Stem Cell Institute, Stanley Center for Psychiatric Research

OpenAlex ID: A5087655955

A Small-Molecule Inhibitor of Tgf-β Signaling Replaces Sox2 in Reprogramming by Inducing Nanog

2009 · Justin K. Ichida, Joel Blanchard, et al. · Cell stem cell · 807

Loss-of-function mutations in the C9ORF72 mouse ortholog cause fatal autoimmune disease

2016 · Aaron Burberry, Naoki Suzuki, et al. · Science Translational Medicine · 269

The mouse C9ORF72 ortholog is enriched in neurons known to degenerate in ALS and FTD

2013 · Naoki Suzuki, Asif M Maroof, et al. · Nature Neuroscience · 77

Nanog-Independent Reprogramming to iPSCs with Canonical Factors

2014 · Ava C. Carter, Brandi N. Davis-Dusenbery, et al. · Stem Cell Reports · 52

Highly efficient neuronal gene knockout in vivo by CRISPR-Cas9 via neonatal intracerebroventricular injection of AAV in mice

2021 · Sam Hana, Michael Peterson, et al. · Gene Therapy · 42

Genetic validation of a therapeutic target in a mouse model of ALS

2014 · A. Sophie de Boer, Kathryn Koszka, et al. · Science Translational Medicine · 36

In vivo genome editing using novel AAV-PHP variants rescues motor function deficits and extends survival in a SOD1-ALS mouse model

2022 · Yi A. Chen, Mark W. Kankel, et al. · Gene Therapy · 30

Efficacy and safety of a SOD1-targeting artificial miRNA delivered by AAV9 in mice are impacted by miRNA scaffold selection

2023 · Shukkwan K. Chen, Zachary C.E. Hawley, et al. · Molecular Therapy — Nucleic Acids · 26

SLC52A3 , A Brown–Vialetto–van Laere syndrome candidate gene is essential for mouse development, but dispensable for motor neuron differentiation

2016 · Atsushi Intoh, Naoki Suzuki, et al. · Human Molecular Genetics · 21

Use of CRISPR/Cas9-mediated disruption of CNS cell type genes to profile transduction of AAV by neonatal intracerebroventricular delivery in mice

2021 · Tess Torregrosa, Sydney Lehman, et al. · Gene Therapy · 20

Expression Pattern of C9ORF72 Ortholog in Mice (S06.004)

2013 · Naoki Suzuki, Asif Maroof, et al. · Neurology

Works count: 11

Citation count: 1,380

H-index: 10

I10-index: 10