Author

Gayatri R Rao

Observed name: Gayatri Rao

Institutions: Cranberry Institute, Phio Pharmaceuticals (United States), X4 Pharmaceuticals, Inc. (United States)

Observed institutions: Cranberry Institute, Phio Pharmaceuticals (United States), Rutgers New Jersey Medical School, X4 Pharmaceuticals, Inc. (United States), University of Medicine and Dentistry of New Jersey

ORCID: 0009-0002-7373-119X

Observed ORCID: 0009-0002-7373-119X

OpenAlex ID: A5110287768

Facilitating Role of Preprotachykinin-I Gene in the Integration of Breast Cancer Cells within the Stromal Compartment of the Bone Marrow

2004 · Gayatri Rao, Prem S. Patel, et al. · Cancer Research · 69

Mosaicism in Fanconi anemia: concise review and evaluation of published cases with focus on clinical course of blood count normalization

2020 · Eileen Nicoletti, Gayatri Rao, et al. · Annals of Hematology · 56

Haematopoietic gene therapy of non-conditioned patients with Fanconi anaemia-A: results from open-label phase 1/2 (FANCOLEN-1) and long-term clinical trials

2024 · Paula Río, Josune Zubicaray, et al. · The Lancet · 35

Natural gene therapy by reverse mosaicism leads to improved hematology in Fanconi anemia patients

2021 · María José Ramírez, Roser Pujol, et al. · American Journal of Hematology · 31

A Phase 1/2 Study of Lentiviral-Mediated Ex-Vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I): Results from Phase 1

2020 · Donald B. Kohn, Gayatri R Rao, et al. · Blood · 15

Lentiviral Mediated Gene Therapy for Pyruvate Kinase Deficiency: A Global Phase 1 Study for Adult and Pediatric Patients

2020 · José Luis López Lorenzo, Susana Navarro, et al. · Blood · 8

A Phase 1/2 Study of Lentiviral-Mediated Ex-Vivo Gene Therapy for Pediatric Patients with Severe Leukocyte Adhesion Deficiency-I (LAD-I): Interim Results

2021 · Donald B. Kohn, Claire Booth, et al. · Blood · 6

Lentiviral-Mediated Gene Therapy for Patients with Fanconi Anemia [Group a]: Updated Results from Global RP-L102 Clinical Trials

2024 · Agnieszka D. Czechowicz, Julián Sevilla, et al. · Blood · 5

Lentiviral Mediated Gene Therapy for Pyruvate Kinase Deficiency: Interim Results of a Global Phase 1 Study for Adult and Pediatric Patients

2021 · Ami J Shah, José Luis López Lorenzo, et al. · Blood · 4

Gene Therapy for Fanconi Anemia [Group A]: Interim Results of RP-L102 Clinical Trials

2021 · Agnieszka Czechowicz, Julián Sevilla, et al. · Blood · 4

RP-L301, a Lentiviral-Mediated Gene Therapy for Pyruvate Kinase Deficiency (PKD): A Phase 2 Clinical Trial Design

2024 · Ami J Shah, José Luis López Lorenzo, et al. · Blood · 1

Allogeneic Hematopoietic Stem Cell Transplantation (allo-HSCT) Outcomes in Leukocyte Adhesion Deficiency Type -I

2024 · Claire Booth, Patrick Gilbert, et al. · Blood

Works count: 12

Citation count: 234

H-index: 6

I10-index: 5