Author

Boer Foekje de

OpenAlex ID: A5153204924

Efficacy and safety results from a pivotal phase 3 trial of DTX401, an AAV8-mediated liver-directed gene therapy, in individuals with glycogen storage disease type Ia (GSDIa)

2025 · John Mitchell, Jose Abdenur, et al. · Endocrine Abstracts · 1

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