A systematic review to evaluate the effectiveness of enzyme replacement therapy for lysosomal storage disorders in comparison to the treatment of similar diseases with higher prevalence
Year: 2014
Type: article
Study design: Systematic Review
Authors: Lang, S.H., Armstrong, N., Noake, C., Kleijnen, J.
Institution: Kleijnen Systematic Reviews (United Kingdom)
Language: English
Subfield: Genetics (clinical)
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W1638895111