Work

Effectiveness of enzyme replacement therapy in 1028 patients with type 1 Gaucher disease after 2 to 5 years of treatment: a report from the Gaucher Registry

Year: 2002

Type: article

Study design: Observational Study

Source: The American Journal of Medicine

DOI: 10.1016/s0002-9343(02)01150-6

Authors: Neal J Weinreb, Joel Charrow, Hans C Andersson, Paige Kaplan, Edwin H Kolodny, Pramod Mistry, Gregory Pastores, Barry E Rosenbloom, C.Ronald Scott, Rebecca S Wappner, Ari Zimran

Institutions: Northwestern University, Lurie Children's Hospital, Tulane University, Children's Hospital of Philadelphia, University of Pennsylvania, New York University, Icahn School of Medicine at Mount Sinai, Cedars-Sinai Medical Center, University of Washington, Riley Hospital for Children, Indiana University Indianapolis, Shaare Zedek Medical Center, Bikur Cholim Hospital

Language: English

Topic: Lysosomal Storage Disorders Research

Subfield: Genetics (clinical)

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W1968758382

FWCI: 14.8

Cites: 48

Cited by: 542

Related to: 10