OpenAlex
PricingAboutJobs
Log inGet started
Work

A follow-up study of MPS I patients treated with laronidase enzyme replacement therapy for 6 years

HTML

Year: 2006
Type: article
Source: Molecular Genetics and Metabolism
DOI: 10.1016/j.ymgme.2006.08.007
Authors: Monica Sifuentes, Robin Doroshow, Richard Hoft, Greg Mason, Irwin Walot, Michael Diament, Susan Okazaki, Kenneth Huff, Gerald F. Cox, Stuart J. Swiedler, Emil D. Kakkis
Institutions: Harbor–UCLA Medical Center, BioMarin (United States)
Language: English

Topic: Lysosomal Storage Disorders Research
Subfield: Physiology
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed

Funder: National Center for Research Resources
Awards: General Clinical Research Center, G939135972
OpenAlex ID: W1990211122
FWCI: 10.5
Cites: 11
Cited by: 219
Related to: 10
OpenAlex
Nonprofit
Open DataOpen Data
Open Source
Product
Search
Compare
Pricing
Repositories
Unpaywall
Unsub
Developers
API docs
Data snapshot
Status
Source code
Organization
About
Team
Testimonials
Brand
Jobs
Community
Help center
Contact
Events
Blog
Mailing list
Supporters
Legal
Privacy
Accessibility
Terms