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Efficacy of hematopoietic stem cell transplantation versus enzyme replacement therapy on brain function in patients with mucopolysaccharidosis type II

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Year: 2014
Type: article
Source: Molecular Genetics and Metabolism
DOI: 10.1016/j.ymgme.2013.12.253
Authors: Akemi Tanaka, Takashi Hamazaki, Torayuki Okuyama, Yasuyuki Suzuki, Norio Sakai, Motomichi Kosuga, Michiko Shinpo, Hiromasa Yabe, Mika Ishige, Hideo Mugishima, Ken Tabuchi, Shunichi Kato
Institutions: Osaka City University, National Center For Child Health and Development, Gifu University, The University of Osaka, Tokai University, Tokyo Metropolitan Komagome Hospital
Language: English

Topic: Lysosomal Storage Disorders Research
Subfield: Physiology
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W1990979815
FWCI:
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Related to: 10
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