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Kinetin in Familial Dysautonomia Carriers: Implications for a New Therapeutic Strategy Targeting mRNA Splicing

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Year: 2009
Type: article
Study design: Clinical Trial
Source: Pediatric Research
DOI: 10.1203/pdr.0b013e318194fd52
Authors: Gabrielle Gold-von Simson, Judith D Goldberg, Linda M Rolnitzky, James Mull, Maire Leyne, Andrei Voustianiouk, Susan A Slaugenhaupt, Felicia B Axelrod
Institutions: New York University, Harvard University, Massachusetts General Hospital
Language: English

Topic: Hereditary Neurological Disorders
Subfield: Cellular and Molecular Neuroscience
Field: Neuroscience
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed

Funders: Dysautonomia Foundation, Deutsches Krebsforschungszentrum, National Institutes of Health, U.S. Public Health Service, National Institute of Neurological Disorders and Stroke, National Center for Research Resources
Awards: G1812960072, G509234630
OpenAlex ID: W2013479387
FWCI: 1.885
Cites: 20
Cited by: 44
Related to: 10
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