Work

Gene therapy in a murine model of methylmalonic acidemia using rAAV9-mediated gene delivery

Year: 2011

Type: article

Source: Gene Therapy

DOI: 10.1038/gt.2011.108

Authors: J S Sénac, R J Chandler, J R Sysol, L Li, C P Venditti

Institutions: National Institutes of Health, National Human Genome Research Institute, George Washington University, National Institute of Diabetes and Digestive and Kidney Diseases

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: green

Funders: National Institutes of Health, National Human Genome Research Institute

Awards: Investigations of Methylmalonic Acidemia and Related Disorders, G5294359063

OpenAlex ID: W2018656452

FWCI: 0.999

Cites: 43

Cited by: 29

Related to: 10