Work

In vitro functional correction of Hermansky–Pudlak Syndrome type-1 by lentiviral-mediated gene transfer

Year: 2014

Type: article

Source: Molecular Genetics and Metabolism

DOI: 10.1016/j.ymgme.2014.11.006

Authors: Yasuhiro Ikawa, Richard Hess, Heidi Dorward, Andrew R. Cullinane, Marjan Huizing, Bernadette R. Gochuico, William A. Gahl, Fabio Candotti

Institutions: National Institutes of Health, National Human Genome Research Institute

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: green

Funders: Université de Lausanne, Centre Hospitalier Universitaire Vaudois, National Institutes of Health, National Human Genome Research Institute

Awards: Gene Therapy Approaches for Primary Immunodeficiencies, G5294359063, Gene Therapy Approaches for Primary Immunodeficiencies, G7881081154

OpenAlex ID: W2019536578

FWCI: 0.873

Cites: 16

Cited by: 17

Related to: 10