Work

Intercellular Transfer of the Virally Derived Precursor Form of Acid α-Glucosidase Corrects the Enzyme Deficiency in Inherited Cardioskeletal Myopathy Pompe Disease

Year: 2001

Type: article

Source: Human Gene Therapy

DOI: 10.1089/104303401300042447

Authors: Daniel F. Pauly, Thomas J. Fraites, Catalin Toma, Helen S. Bayes, Maryann L. Huie, Rochelle Hirschhorn, Paul H. Plotz, Nina Raben, Paul D. Kessler, Barry J. Byrne

Institutions: Johns Hopkins University, Johns Hopkins Medicine, University of Florida, Johns Hopkins Hospital, University of Florida Health, NYU Langone Health, New York University, National Institutes of Health, National Institute of Arthritis and Musculoskeletal and Skin Diseases

Language: English

Topic: Lysosomal Storage Disorders Research

Subfield: Physiology

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

Funders: American Heart Association, Johns Hopkins University, National Institutes of Health, National Heart, Lung, and Blood Institute, Eunice Kennedy Shriver National Institute of Child Health and Human Development

Awards: G1142261105, G1191055758, G1965936037, CALCIUM ION CONTROL IN CARDIAC FUNCTION

OpenAlex ID: W2020970293

FWCI: 2.59

Cites: 43

Cited by: 50

Related to: 10