Work

A Pilot Study of In Vivo Liver-Directed Gene Transfer with an Adenoviral Vector in Partial Ornithine Transcarbamylase Deficiency

Year: 2002

Type: article

Study design: Clinical Trial

Source: Human Gene Therapy

DOI: 10.1089/10430340152712719

Authors: Steven E. Raper, Marc Yudkoff, Narendra Chirmule, Guang-Ping Gao, Fred Nunes, Ziv J. Haskal, Emma E. Furth, Kathleen J. Propert, Michael B. Robinson, Susan Magosin, Heather Simoes, Lisa Speicher, Joseph Hughes, John Tazelaar, Nelson A. Wivel, James M. Wilson, Mark L. Batshaw

Institutions: University of Pennsylvania, Children's Hospital of Philadelphia, Children's National, George Washington University

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: closed

Funders: National Institutes of Health, U.S. Food and Drug Administration, National Institute of Diabetes and Digestive and Kidney Diseases, National Center for Research Resources, Eunice Kennedy Shriver National Institute of Child Health and Human Development

Awards: GENE THERAPY FOR ORNITHINE TRANSCARBAMYLASE DEFICIENCY, G1547288941, Molecular Therapy for Cystic Fibrosis, GENERAL CLINICAL RESEARCH CENTER, G7340929987

OpenAlex ID: W2023254910

FWCI: 16.97

Cites: 50

Cited by: 351

Related to: 10