Enzyme replacement and enhancement therapies: lessons from lysosomal disorders
Year: 2002
Type: review
Source: Nature Reviews Genetics
DOI: 10.1038/nrg963
Authors: Robert J. Desnick, Edward H. Schuchman
Institutions: New York University, Icahn School of Medicine at Mount Sinai
Language: English
Subfield: Genetics (clinical)
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W2024420787
