Work

Vision 1 Year after Gene Therapy for Leber's Congenital Amaurosis

Year: 2009

Type: article

Abstract: To the Editor: Leber's congenital amaurosis, a common cause of blindness in infants and children,1 recently became the first human genetic retinal disease to show improved vision in response to tre...

Source: New England Journal of Medicine

DOI: 10.1056/nejmc0903652

Authors: Artur V. Cideciyan, William W. Hauswirth, Tomas S. Aleman, Shalesh Kaushal, Sharon B. Schwartz, Sanford L. Boye, Elizabeth A.M. Windsor, Thomas J. Conlon, Alexander Sumaroka, Alejandro J. Roman, Barry J. Byrne, Samuel G. Jacobson

Institutions: University of Pennsylvania, University of Florida

Language: English

Topic: Retinal Development and Disorders

Subfield: Ophthalmology

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: bronze

Funder: National Eye Institute

Award: Clinical Trials of Gene Therapy for Leber Congenital Amaurosis

OpenAlex ID: W2056320636

FWCI: 22

Cites: 5

Cited by: 206

Related to: 10