A phase I trial of adeno-associated virus serotype 1-γ-sarcoglycan gene therapy for limb girdle muscular dystrophy type 2C
Year: 2011
Type: article
Study design: Clinical Trial
Source: Brain
DOI: 10.1093/brain/awr342
Authors: Serge Herson, Faycal Hentati, Aude Rigolet, Anthony Behin, Norma B. Romero, France Leturcq, Pascal Laforêt, Thierry Maisonobe, Rim Amouri, Hafedh Haddad, Muriel Audit, Marie Montus, Carole Masurier, Bernard Gjata, Christophe Georger, Mustapha Cheraï, Pierre Carlier, Jean-Yves Hogrel, Ariane Herson, Yves Allenbach, François M. Lemoine, David Klatzmann, H. Lee Sweeney, Richard C. Mulligan, Bruno Eymard, Didier Caizergues, Thomas Voït, Olivier Benveniste
Institutions: Assistance Publique – Hôpitaux de Paris, Pitié-Salpêtrière Hospital, Université Pierre-et-Marie-Curie, National Institute of Neurology Mongi-Ben Hamida, Institut de Myologie, Hôpital Cochin, Genethon (France), GenoSafe, Centre National de la Recherche Scientifique, University of Pennsylvania, Harvard University
Language: English
Subfield: Genetics
Domain: Life Sciences
Open Access status: closed
Funder: Medical Research Council
OpenAlex ID: W2066619852