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Transplantation of Genetically Corrected Human iPSC-Derived Progenitors in Mice with Limb-Girdle Muscular Dystrophy

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Year: 2012
Type: article
Source: Science Translational Medicine
DOI: 10.1126/scitranslmed.3003541
Authors: Francesco Saverio Tedesco, Mattia F. M. Gerli, Laura Perani, Sara Benedetti, Federica Ungaro, Marco Cassano, Stefania Antonini, Enrico Tagliafico, Valentina Artusi, Emanuela Longa, Rossana Tonlorenzi, Martina Ragazzi, Giorgia Calderazzi, Hidetoshi Hoshiya, Ornella Cappellari, Marina Mora, Benedikt Schoser, Peter Schneiderat, Mitsuo Oshimura, Roberto Bottinelli, Maurilio Sampaolesi, Yvan Torrente, Vania Broccoli, Giulio Cossu
Institutions: University College Hospital, University College London Hospitals NHS Foundation Trust, IRCCS Ospedale San Raffaele, University College London, KU Leuven, University of Milan, University of Modena and Reggio Emilia, University of Pavia, Fondazione Salvatore Maugeri, Fondazione IRCCS Istituto Neurologico Carlo Besta, Ludwig-Maximilians-Universität München, Tottori University
Language: English

Topic: Muscle Physiology and Disorders
Subfield: Molecular Biology
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W2074283287
FWCI: 11.06
Cites: 44
Cited by: 310
Related to: 10
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