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Ribozyme rescue of photoreceptor cells in P23H transgenic rats: Long-term survival and late-stage therapy
Work
Year: 2000
Type: article
Abstract: Ribozyme-directed cleavage of mutant mRNAs appears to be a potentially effective therapeutic measure for dominantly inherited diseases. We previously demonstrated that two ribozymes targeted to the P2... more
Cites: 39
Cited by: 204
Related to: 10
FWCI: 5.189
Citation percentile (by year/subfield): 91.53
Sustainable Development Goal Good health and well-being
Open Access status: green