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Multivalent N -Acetylgalactosamine-Conjugated siRNA Localizes in Hepatocytes and Elicits Robust RNAi-Mediated Gene Silencing

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Year: 2014
Type: article
Source: Journal of the American Chemical Society
DOI: 10.1021/ja505986a
Authors: Jayaprakash K. Nair, Jennifer L. S. Willoughby, Amy Chan, Klaus Charisse, Md. Rowshon Alam, Qianfan Wang, Menno Hoekstra, Pachamuthu Kandasamy, Alexander V. Kel’in, Stuart Milstein, Nate Taneja, Jonathan O’Shea, Sarfraz Shaikh, Ligang Zhang, Ronald J. van der Sluis, Michael E. Jung, Akin Akinc, Renta Hutabarat, Satya Kuchimanchi, Kevin Fitzgerald, Tracy Zimmermann, Theo J. C. van Berkel, Martin A. Maier, Kallanthottathil G. Rajeev, Muthiah Manoharan
Institutions: Alnylam Pharmaceuticals (United States), Leiden University, University of California, Los Angeles
Language: English

Topic: RNA Interference and Gene Delivery
Subfield: Molecular Biology
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W2078890343
FWCI: 21.81
Cites: 38
Cited by: 1,170
Related to: 10
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