Work

Early gestational gene transfer with targeted ATP7B expression in the liver improves phenotype in a murine model of Wilson's disease

Year: 2011

Type: article

Source: Gene Therapy

DOI: 10.1038/gt.2011.186

Authors: J L Roybal, M Endo, A Radu, L Gray, C A Todorow, P W Zoltick, S Lutsenko, A W Flake

Institutions: Children's Hospital of Philadelphia, Johns Hopkins University

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: closed

Funders: National Institutes of Health, National Institute of General Medical Sciences, Eunice Kennedy Shriver National Institute of Child Health and Human Development

Awards: Fetal Biology and Therapy Training Program, Mechanisms of metal ion regulation in human cells

OpenAlex ID: W2092588757

FWCI: 1.394

Cites: 36

Cited by: 43

Related to: 10