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Therapeutic silencing of an endogenous gene by systemic administration of modified siRNAs

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Year: 2004
Type: article
Source: Nature
DOI: 10.1038/nature03121
Authors: Jürgen Soutschek, Akin Akinc, Birgit Bramlage, Klaus Charisse, Rainer Constien, Mary Donoghue, Sayda Elbashir, Anke Geick, Philipp Hadwiger, Jens Harborth, Matthias John, Venkitasamy Kesavan, Gary Lavine, Rajendra K. Pandey, Timothy Racie, Kallanthottathil G. Rajeev, Ingo Röhl, Ivanka Toudjarska, Gang Wang, Silvio Wuschko, David Bumcrot, Victor Koteliansky, Stefan Limmer, Muthiah Manoharan, Hans-Peter Vornlocher
Institution: Alnylam Pharmaceuticals (United States)
Language: English

Topic: RNA Interference and Gene Delivery
Subfield: Molecular Biology
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W2116424844
FWCI: 44.46
Cites: 22
Cited by: 2,211
Related to: 10
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