Work

Novel oral treatment of Gaucher's disease with N-butyldeoxynojirimycin (OGT 918) to decrease substrate biosynthesis

Year: 2000

Type: article

Study design: Clinical Trial

Source: The Lancet

DOI: 10.1016/s0140-6736(00)02161-9

Authors: Timothy Cox, Robin Lachmann, Carla Hollak, Johannes Aerts, Sonja van Weely, Martin Hrebícek, Frances Platt, Terry Butters, Raymond Dwek, Chris Moyses, Irene Gow, Deborah Elstein, Ari Zimran

Institutions: University of Cambridge, Addenbrooke's Hospital, Amsterdam UMC Location University of Amsterdam, University of Amsterdam, University of Oxford, Shaare Zedek Medical Center

Language: English

Topic: Lysosomal Storage Disorders Research

Subfield: Genetics (clinical)

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

Funders: Wellcome Trust, University of Oxford, Lister Institute of Preventive Medicine

OpenAlex ID: W2135424735

FWCI: 22.64

Cites: 26

Cited by: 752

Related to: 10