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Functional amelioration of murine galactosialidosis by genetically modified bone marrow hematopoietic progenitor cells

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Year: 2002
Type: article
Source: Blood
DOI: 10.1182/blood.v99.9.3169
Authors: Thasia Leimig, Linda Mann, Maria del Pilar Martin, Erik Bonten, Derek Persons, James Knowles, James A. Allay, John Cunningham, Arthur W. Nienhuis, Richard Smeyne, Alessandra d'Azzo
Institution: St. Jude Children's Research Hospital
Language: English

Topic: Lysosomal Storage Disorders Research
Subfield: Genetics (clinical)
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed

Funders: National Cancer Institute, National Institute of Diabetes and Digestive and Kidney Diseases
Awards: GM1 as apoptotic signal in neurodegenerative GM1-gangliosidosis, Cancer Center Support Grant (CCSG)
OpenAlex ID: W2141080862
FWCI: 5.338
Cites: 49
Cited by: 75
Related to: 10
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