Work

Miglustat for treatment of Niemann-Pick C disease: a randomised controlled study

Year: 2007

Type: article

Study designs: Randomized Controlled Trial, Clinical Trial

Source: The Lancet Neurology

DOI: 10.1016/s1474-4422(07)70194-1

Authors: Marc C Patterson, Darleen Vecchio, Helena Prady, Larry Abel, James E Wraith

Institutions: Columbia University, Royal Manchester Children's Hospital, The University of Melbourne

Language: English

Topic: Lysosomal Storage Disorders Research

Subfield: Genetics (clinical)

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: green

Funder: Actelion Pharmaceuticals

OpenAlex ID: W2155503300

FWCI: 21.84

Cites: 38

Cited by: 619

Related to: 9