Pharmacokinetic profile of recombinant human N-acetylgalactosamine 4-sulphatase enzyme replacement therapy in patients with mucopolysaccharidosis VI (Maroteaux–Lamy syndrome): a phase I/II study
Year: 2005
Type: article
Source: Acta Paediatrica
Authors: P Harmatz, W G Kramer, J J Hopwood, J Simon, E Butensky, S J Swiedler, on behalf of the Mucopolysaccharidosis VI Study Group
Institutions: Women's and Children's Hospital, BioMarin (United States)
Language: English
Subfield: Physiology
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W4235853962