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Controlling AAV Tropism in the Nervous System with Natural and Engineered Capsids

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Year: 2015
Type: book-chapter
Source: Methods in molecular biology
DOI: 10.1007/978-1-4939-3271-9_10
Authors: Michael J. Castle, Heikki T. Turunen, Luk H. Vandenberghe, John H. Wolfe
Institutions: Children's Hospital of Philadelphia, University of California San Diego, Massachusetts Eye and Ear Infirmary, Harvard University, University of Pennsylvania
Language: English

Topic: Virus-based gene therapy research
Subfield: Genetics
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: green

Funders: National Institutes of Health, National Institute of Diabetes and Digestive and Kidney Diseases, National Institute of Neurological Disorders and Stroke, Eunice Kennedy Shriver National Institute of Child Health and Human Development
Awards: Broad Spectrum Molecular Therapy for Blinding Retina Disorders, Disseminated AAV Vector Transport in the Brain Via Neuronal Pathways, Choroid Plexus-Directed Gene Therapy for Alpha-Mannosidosis, Training Program in Neurodevelopmental Disabilities, Gene Transfer and NMR Studies in Alpha-Mannosidosis Brain
OpenAlex ID: W2176154815
FWCI: 23.16
Cites: 134
Cited by: 149
Related to: 10
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