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IPSC-derived dopaminergic neurons from patients with Gaucher disease and Parkinsonism demonstrate the potential of a new glucocerebrosidase chaperone

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Year: 2016
Type: article
Source: Molecular Genetics and Metabolism
DOI: 10.1016/j.ymgme.2015.12.162
Authors: Elma Aflaki, Daniel K. Borger, Nima Moaven, Barbara K. Stubblefield, Steven A. Rogers, Samarjit Patnaik, Wendy Westbroek, Patricia Sullivan, Hideji Fujiwara, Grisel Lopez, David S. Goldstein, Daniel S. Ory, Juan Marugan, Ellen Sidransky
Institutions: National Institutes of Health, National Human Genome Research Institute, University of Kansas, National Center for Advancing Translational Sciences, National Institute of Neurological Disorders and Stroke, Washington University in St. Louis
Language: English

Topic: Lysosomal Storage Disorders Research
Subfield: Physiology (medical)
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W2258436151
FWCI:
Cites:
Cited by: 1
Related to: 10
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