OpenAlex
PricingAboutJobs
Log inGet started
Work

Novel treatment for Fabry disease: IV administration of plant derived alpha-gal-A enzyme safety and efficacy interim report

HTML

Year: 2016
Type: article
Study design: Observational Study
Source: Molecular Genetics and Metabolism
DOI: 10.1016/j.ymgme.2015.12.296
Authors: Derralynn Hughes, Simeon Boyd, Pilar Giraldo, Derlis Gonzalez, Myrl Holida, Ozlem Goker-Alpan, Gustavo Megawa, Mohamed Atta, Kathy Nicholls, Raphael Schiffmann, Ahmad Tuffaha, Jeannie Visootsak, Laura Barisoni, Robert Colvin, J. Charles Jannette, Sari Alon, Jenny Krupko, Mali Szlaifer, Einat Brill-Almon, Raul Chertkoff
Institutions: University College London, University of California Davis Medical Center, Instituto Privado de Hematología e Investigación Clínica, University of Iowa Hospitals and Clinics, O&O Alpan (United States), Johns Hopkins University, The Royal Melbourne Hospital, University of Kansas Medical Center, Emory University Hospital, University of Miami, Massachusetts General Hospital, University of North Carolina at Chapel Hill, Protalix BioTherapeutics (Israel)
Language: English

Topic: Lysosomal Storage Disorders Research
Subfield: Physiology
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W2260718243
FWCI:
Cites:
Cited by: 2
Related to: 10
OpenAlex
Nonprofit
Open DataOpen Data
Open Source
Product
Search
Compare
Pricing
Repositories
Unpaywall
Unsub
Developers
API docs
Data snapshot
Status
Source code
Organization
About
Team
Testimonials
Brand
Jobs
Community
Help center
Contact
Events
Blog
Mailing list
Supporters
Legal
Privacy
Accessibility
Terms