Work

Intranasal gene delivery of AAV9 iduronidase: A non-invasive and effective gene therapy approach for prevention of neurologic disease in a murine model of mucopolysaccharidosis type I

Year: 2016

Type: article

Source: Molecular Genetics and Metabolism

DOI: 10.1016/j.ymgme.2015.12.195

Authors: Lalitha Belur, Megan Buckvold, Kelly M. Podetz-Pedersen, Maureen Riedl, Lucy Vulchanova, Leah R. Hanson, Carolyn Fairbanks, Karen Kozarsky, William H. Frey, Walter C. Low, R. Scott McIvor

Institutions: University of Minnesota, Regions Hospital, Regenxbio (United States)

Language: English

Topic: Lysosomal Storage Disorders Research

Subfield: Physiology

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W2263275941

FWCI:

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