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P1.33 Disease progression observed in clinical outcome measures in placebo-treated patients with nonsense mutation dystrophinopathy

Year: 2011

Type: article

Source: Neuromuscular Disorders

DOI: 10.1016/j.nmd.2011.06.793

Authors: E. Mercuri, K. Bushby, C. McDonald, N. Goemans, F. Muntoni, B.T. Darras, G.L. Elfring, J. Barth, A. Reha, S.W. Peltz

Institutions: Università Cattolica del Sacro Cuore, Centre for Life, Newcastle University, University of California, Davis, Universitair Ziekenhuis Leuven, Great Ormond Street Hospital, Boston Children's Hospital, Harvard University, PTC Therapeutics (United States)

Language: English

Topic: Muscle Physiology and Disorders

Subfield: Molecular Biology

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W2288949219

FWCI: 0.129

Cites:

Cited by: 1

Related to: 10