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Efficient Mitochondrial Import of Newly Synthesized Ornithine Transcarbamylase (OTC) and Correction of Secondary Metabolic Alterations in spfash Mice following Gene Therapy of OTC Deficiency

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Year: 1999
Type: article
Source: Molecular Medicine
DOI: 10.1007/bf03402122
Authors: Klaus Peter Zimmer, Meike Bendiks, Masataka Mori, Eiki Kominami, Michael B. Robinson, Xuehai Ye, James M. Wilson
Institutions: University Hospital Münster, Kumamoto University, Juntendo University, Children's Hospital of Philadelphia, University of Pennsylvania Health System, The Wistar Institute
Language: English

Topic: Metabolism and Genetic Disorders
Subfield: Clinical Biochemistry
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: bronze

Funders: Deutsche Forschungsgemeinschaft, National Institutes of Health, National Institute of Diabetes and Digestive and Kidney Diseases, Eunice Kennedy Shriver National Institute of Child Health and Human Development
Awards: GENE THERAPY FOR ORNITHINE TRANSCARBAMYLASE DEFICIENCY, Molecular Therapy for Cystic Fibrosis
OpenAlex ID: W233537767
FWCI: 0.682
Cites: 21
Cited by: 8
Related to: 10
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