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Successful Gene Therapy in Utero for Lethal Murine Hypophosphatasia

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Year: 2011
Type: article
Source: Human Gene Therapy
DOI: 10.1089/hum.2011.148
Authors: Hanako Sugano, Tae Matsumoto, Koichi Miyake, Atsushi Watanabe, Osamu Iijima, Makoto Migita, Sonoko Narisawa, José Luis Millán, Yoshitaka Fukunaga, Takashi Shimada
Institutions: Nippon Medical School, Sanford Burnham Prebys Medical Discovery Institute
Language: English

Topic: Alkaline Phosphatase Research Studies
Subfield: Endocrinology, Diabetes and Metabolism
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed

Funders: University of Pennsylvania, National Institutes of Health, Japan Society for the Promotion of Science, National Institute of Dental and Craniofacial Research
Awards: Perinatal gene therapy for severe genetic diseases, G6110899351, G701293452, G9000275929
OpenAlex ID: W2353695153
FWCI: 1.651
Cites: 33
Cited by: 44
Related to: 10
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