Delivery of an Adeno-Associated Virus Vector into Cerebrospinal Fluid Attenuates Central Nervous System Disease in Mucopolysaccharidosis Type II Mice
Year: 2016
Type: article
Source: Human Gene Therapy
DOI: 10.1089/hum.2016.101
Authors: Christian Hinderer, Nathan Katz, Jean-Pierre Louboutin, Peter Bell, Hongwei Yu, Mohamad Nayal, Karen Kozarsky, W. Timothy O'Brien, Tamara Goode, James M. Wilson
Language: English
Subfield: Physiology
Field: Medicine
Domain: Health Sciences
Open Access status: closed
Funder: REGENXBIO
OpenAlex ID: W2491807813