322. Genome Editing for Nucleotide Repeat Disorders: Towards a New Therapeutic Approach for Myotonic Dystrophy Type 1
Work
Year: 2016
Type: article
Abstract: Myotonic dystrophy type 1 (DM1) belongs to the group of nucleotide repeat disorders. More specifically this autosomal form of muscular dystrophy is caused by the expansion of the CTG trinucleotide rep... more
Source: Molecular Therapy
Institutions Genethon (France), Inserm, Délégation Paris 5, Sorbonne Paris Cité, Université Paris Cité +4 more
Cites:
Cited by: 1
Related to: 10
FWCI: 0.134
Citation percentile (by year/subfield): 34.76
Subfield: Cellular and Molecular Neuroscience
Field: Neuroscience
Domain: Life Sciences
Sustainable Development Goal Good health and well-being
Open Access status: hybrid
APC paid (est): $3,900