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Clinical-Scale Genome Editing of the Human BCL11A Erythroid Enhancer for Treatment of the Hemoglobinopathies

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Year: 2015
Type: article
Source: Blood
DOI: 10.1182/blood.v126.23.204.204
Authors: Fyodor D Urnov, Andreas Reik, Jeff Vierstra, Kai-Hsin Chang, Yuanyue Zhou, Andrea Mich, Jennifer Adrian, Lisa Fox, Nikoletta Psatha, Siyuan Tan, Evangelia Yannaki, Stewart Craig, Edward J. Rebar, John Stamatoyannopoulos, Thalia Papayannopoulou, George Stamatoyannopoulos, Haiyan Jiang
Institutions: Sangamo BioSciences (United States), University of Washington, Biogen (United States), G. Papanikolaou General Hospital
Language: English

Topic: Hemoglobinopathies and Related Disorders
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W2581247422
FWCI: 1.145
Cites:
Cited by: 10
Related to: 10
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