rAAV-mediated gene transfer of a truncated CFTR rescues the cystic fibrosis phenotype in human intestinal organoids and CF mice
Year: 2015
Type: article
Source: Lirias
Authors: Dragana Vidović, Marianne Carlon, Mélanie Faria da Cunha, Johanna Dekkers, Monika I. Hollenhorst, Marcel J. C. Bijvelds, Anabela S. Ramalho, Chris Van den Haute, Veerle Baekelandt, K. De Boeck, Isabelle Sermet‐Gaudelus, Hugo de Jonge, Jeffrey M. Beekman, Aleksander Edelman, Rik Gijsbers, Zeger Debyser
Language: English
Subfield: Pulmonary and Respiratory Medicine
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W2593261256
