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Assessment of Insertional Mutagenesis Risk Following AAV Vector-Mediated Factor IX Gene Transfer in Mice.

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Year: 2009
Type: article
Source: Blood
DOI: 10.1182/blood.v114.22.2465.2465
Authors: Hojun Li, Nirav Malani, Shari R Hamilton, Alexander Schlachterman, Jim Z Zhang, Giulio Bussadori, Shyrie A Edmonson, Federico Mingozzi, J. Fraser Wright, Valder R. Arruda, Frederic D Bushman, Katherine A. High
Institutions: Children's Hospital of Philadelphia, University of Pennsylvania, University of Missouri, Howard Hughes Medical Institute
Language: English

Topic: Virus-based gene therapy research
Subfield: Genetics
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W2593319044
FWCI:
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Related to: 10
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