Work

Lentiglobin Gene Therapy for Transfusion-Dependent β-Thalassemia: Update from the Northstar Hgb-204 Phase 1/2 Clinical Study

Year: 2016

Type: article

Study design: Clinical Trial

Source: Blood

DOI: 10.1182/blood.v128.22.1175.1175

Authors: Alexis A. Thompson, Janet Kwiatkowski, John Rasko, Suradej Hongeng, Gary J. Schiller, Usanarat Anurathapan, Marina Cavazzana, P. Joy Ho, Christof von Kalle, Morris Kletzel, Philippe Leboulch, Elliott Vichinsky, Alexandria Petrusich, Mohammed Asmal, Mark C. Walters

Institutions: Lurie Children's Hospital, Children's Hospital of Philadelphia, Royal Prince Alfred Hospital, Mahidol University, Ramathibodi Hospital, University of California, Los Angeles, Inserm, Assistance Publique – Hôpitaux de Paris, German Cancer Research Center, National Center for Tumor Diseases, Northwestern University, Université Paris-Sud, Brigham and Women's Hospital, Harvard University, Commissariat à l'Énergie Atomique et aux Énergies Alternatives, CEA Paris-Saclay - Etablissement de Fontenay-aux-roses, UCSF Benioff Children's Hospital, Bluebird Bio (United States)

Language: English

Topic: Virus-based gene therapy research

Subfield: Genetics

Field: Biochemistry, Genetics and Molecular Biology

Domain: Life Sciences

SDG: Good health and well-being

Open Access status: closed

OpenAlex ID: W2613798932

FWCI: 4.249

Cites:

Cited by: 24

Related to: 10