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Transformative therapies for rare CFTR missense alleles

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Year: 2017
Type: review
Source: Current Opinion in Pharmacology
DOI: 10.1016/j.coph.2017.09.018
Authors: Kathryn E Oliver, Sangwoo T Han, Eric J Sorscher, Garry R Cutting
Institutions: Emory University, Children's Healthcare of Atlanta, Johns Hopkins University, Johns Hopkins Medicine
Language: English

Topic: Cystic Fibrosis Research Advances
Subfield: Pulmonary and Respiratory Medicine
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: green

Funders: Cystic Fibrosis Foundation, National Heart, Lung, and Blood Institute, National Institute of General Medical Sciences, National Institute of Diabetes and Digestive and Kidney Diseases
Awards: G276595759, G3280268463, G458068826, G5245754397, Modulation of Ribosome Dynamics Rescues F508del CFTR Maturational Arrest, G6228051903, G7620752923, UAB CF Research and Translation Core Center, Molecular Genetics of Cystic Fibrosis
OpenAlex ID: W2761392816
FWCI: 0.799
Cites: 51
Cited by: 22
Related to: 10
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