Work

Attenuation of the Niemann-Pick type C2 disease phenotype by intracisternal administration of an AAVrh.10 vector expressing Npc2

Year: 2018

Type: article

Source: Experimental Neurology

DOI: 10.1016/j.expneurol.2018.04.001

Authors: Sandra Markmann, Jasmine J. Christie-Reid, Jonathan B. Rosenberg, Bishnu P. De, Stephen M. Kaminsky, Ronald G. Crystal, Dolan Sondhi

Institution: Weill Cornell Medicine

Language: English

Topic: Lysosomal Storage Disorders Research

Subfield: Physiology (medical)

Field: Medicine

Domain: Health Sciences

SDG: Good health and well-being

Open Access status: closed

Funders: Weill Cornell Medical College, Albert Einstein College of Medicine, Yeshiva University

OpenAlex ID: W2797251557

FWCI: 1.662

Cites: 71

Cited by: 21

Related to: 10