AVXS-101 Phase 1 Gene Therapy Clinical Trial in SMA Type 1: Event Free Survival and Achievement of developmental milestones (CT.003)
Year: 2017
Type: article
Study design: Clinical Trial
Source: Neurology
Authors: Jerry Mendell, Samiah A. Al-Zaidy, Richard Shell, W. David Arnold, Louise R. Rodino-Klapac, Thomas W. Prior, Linda Lowes, Lindsay N. Alfano, Katherine Berry, Kathleen Church, John Kissel, Sukumar Nagendran, James L’Italien, Doug M. Sproule, Minna Du, Jessica A. Cardenas, Arthur Burghes, Kevin D. Foust, Kathrin Meyer, Shibi Likhite, Brian K. Kaspar
Institutions: Nationwide Children's Hospital, The Ohio State University
Language: English
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
Open Access status: closed
OpenAlex ID: W2804665224