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Ambulatory function and fatigue in nusinersen-treated children with spinal muscular atrophy. (P2.322)

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Year: 2018
Type: article
Source: Neurology
DOI: 10.1212/wnl.90.15_supplement.p2.322
Authors: Jacqueline Montes, Sally Dunaway Young, Elena Mazzone, Amy Pasternak, Allan Glanzman, Richard Finkel, Basil Darras, Francesco Muntoni, Eugenio Mercuri, Darryl De Vivo, Kathie Bishop, Eugene Schneider, Frank Bennett, Richard Foster, Wildon Farwell
Institutions: Columbia University Irving Medical Center, Boston Children's Hospital, Children's Hospital of Philadelphia, Nemours Children's Clinic, Harvard University, University College London, Ionis Pharmaceuticals (United States), Biogen (United States)
Language: English

Topic: Neurogenetic and Muscular Disorders Research
Subfield: Genetics
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W2804939566
FWCI: 0.709
Cites:
Cited by: 5
Related to: 10
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