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Outcomes for Initial Patient Cohorts with up to 33 Months of Follow-up in the Hgb-206 Phase 1 Trial

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Year: 2018
Type: conference-abstract
Source: Blood
DOI: 10.1182/blood-2018-99-113477
Authors: Julie Kanter, John F. Tisdale, Janet L. Kwiatkowski, Lakshmanan Krishnamurti, Markus Y. Mapara, Manfred Schmidt, Alexandra L. Miller, Francis J. Pierciey, Weiliang Shi, Jean-Antoine Ribeil, Mark C. Walters, Alexis A. Thompson
Institutions: Medical University of South Carolina, National Institutes of Health, National Institute of Diabetes and Digestive and Kidney Diseases, National Heart, Lung, and Blood Institute, Children's Hospital of Philadelphia, University of Pennsylvania, Emory University, Columbia University, Bluebird Bio (United States), UCSF Benioff Children's Hospital, Northwestern University, Lurie Children's Hospital
Language: English

Topic: Virus-based gene therapy research
Subfield: Genetics
Field: Biochemistry, Genetics and Molecular Biology
Domain: Life Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W2906725115
Cites:
Cited by: 14
Related to: 10
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