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CRISPR/Cas9 Gene-Edited Hematopoietic Stem Cell Therapy for Sickle Cell Disease

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Year: 2017
Type: article
Source: Blood
DOI: 10.1182/blood.v130.suppl_1.535.535
Authors: Vionnie W.C. Yu, Yi Liu, Matthew Curran, Pu Zhang, Jennifer L. Snead, Christian Schmedt, Yi Yang, Victor Guosheng Lin, William R. Tschantz, Lisa Quinn, Carsten Russ, Scott Clarkson, Amy Janiak, Morag Stewart, Yanick Mulumba, Reynald Lescarbeau, Brad Murray, Jessica Seitzer, Walter Strapps, Hon-Ren Huang, Kevin L. Sloan, Craig Mickanin, Lloyd B. Klickstein, Susan C. Stevenson
Institutions: Novartis Institutes for BioMedical Research, Beth Israel Deaconess Medical Center, Harvard University, Genomics Institute of the Novartis Research Foundation, Intellia Therapeutics (United States)
Language: English

Topic: Hemoglobinopathies and Related Disorders
Subfield: Genetics (clinical)
Field: Medicine
Domain: Health Sciences
SDG: Good health and well-being

Open Access status: closed
OpenAlex ID: W2906725216
FWCI: 0.699
Cites:
Cited by: 6
Related to: 10
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